New study offers hope for patients suffering from a rare form of blindness

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October 31, 2018

Neuroscience Rare Diseases

Translational Research

Grantee

A new form of therapy may halt or even reverse a form of progressive vision loss that, until now, has inevitably led to blindness. This hyper-targeted approach offers hope to individuals living with spinocerebellar ataxia type 7 (SCA7) and validates a new form of therapy with the potential to treat neurogenetic diseases effectively and with far fewer side effects than other medications.